Abu Dhabi has become the first city in the world to administer ITVISMA (onasemnogene abeparvovec), a breakthrough gene therapy for spinal muscular atrophy (SMA). The treatment was successfully delivered at Sheikh Khalifa Medical City under the supervision of the Department of Health – Abu Dhabi.
A three-year-old boy, Oliver Chu, becomes the first patient in the world to receive a revolutionary gene therapy for Hunter syndrome, a rare genetic disorder. After the groundbreaking treatment in Manchester, doctors report astonishing progress in his physical and cognitive development, offering new hope for children with rare diseases.
Vinay Prasad, a senior regulator at the US Food and Drug Administration, has stepped down from his position amid controversy over the agency’s handling of Sarepta Therapeutics Inc.’s gene therapy.
29 Dec 2025-11:59
30 Jul 2025-11:29
